Question

Do ADA deficient patients need repeated blood transfusion?

Answer 1

Answer:

Enzyme-replacement therapy is effective in most patients with ADA deficiency2 but often fails to sustain lymphocyte counts and T-cell function. We found that ADA gene therapy improves immune function in patients who had insufficient immune reconstitution during PEG-ADA therapy.

Explanation:

Answer 2

Answer:

i know gene therapy cure the ada deficiency in embroynic stage ada deficiency fully cure by bone marrow transplanation