Question

Read the following article regarding “Gene therapy” and answer the following questions. The ultimate goal of gene therapy is the gene replacement therapy. Gene replacement therapy permits physiological regulation of the transgenes and elimination of the possibility of insertional activation of other cellular gene which occur at the time of random integration of the foreign gene. At present the current strategy for gene therapy largely centres around gene augmentatious therapy, where the foreign gene replaces the defections or missing gene.(a) What is gene therapy?(b) How is gene therapy being used in treating ADA deficiency patients?(c) Mention the cause and the body system affected by ADA deficiency in humans.(d) Name the vector use for transferring ADA-DNA into the recipients cells in humans. Name the recipients cells.

Answer 1

a replacement thearapy b forign gene