Question

what is meant by Ada deficiency? how is gene therapy a solution to this problem?why is it not a permanent cure?

Answer 1

Adenosine deaminase deficiency (also called ADA deficiency or ADA-SCID) is an autosomal recessive metabolic disorder that causes immunodeficiency. It occurs in fewer than one in 100,000 live births worldwide. It accounts for about 15% of all cases of severe combined immunodeficiency (SCID)